Promising gene therapy delivers treatment directly to brain

Rylae-Ann Poulin attends physical education class at Ruamrudee International School in Bangkok, Thailand, Friday, Jan. 13, 2023. A treatment Rylae-Ann received recently became the first brain-delivered gene therapy on the market after its approval in Europe and the U.K. for AADC deficiency, a disorder that interferes with the way cells in the nervous system communicate. (AP Photo/Sakchai Lalit)

Promising gene therapy delivers treatment directly to brain